Finding Better Treatments for Rare Disease
About 7,000 rare diseases affect 30 million Americans. Two-thirds of those affected are children.
At Sanford Research, we’re working to improve treatment of rare and pediatric diseases – neurodegenerative diseases including Batten disease, ciliary-associated disorders, kidney diseases and many more.
Our work includes:
- Understanding the genetic, cellular and molecular development of organs and disease
- Developing and testing effective therapies in the lab and clinical trials
By uncovering the causes of rare and childhood disorders, we can create better ways to treat them.
The Pediatrics and Rare Diseases Group supports:
- NIH funded Pediatric Research Center of Biomedical Research Excellence
- Coordination of Rare Diseases at Sanford (CoRDS)
- NIH-supported Neonatal Research Network
Primary Faculty
Secondary Faculty
Sanford Health News
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Sanford Health joins Undiagnosed Diseases Network
Sanford plans to enroll at least five patients each year who meet criteria
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How to create simple science fun at home
Encourage your child’s love of exploring and discovering with easy activities
Classes & Events
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From Nature to Molecules: Engaging Biology PD for Inspired Teaching
Mon 07/14/25 12:00 AM - Thu 07/17/25 12:00 AM
Sanford Research Center